TURCHIANO, GIANDOMENICO

TURCHIANO, GIANDOMENICO  

Dipartimento di Scienze della Vita  

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Titolo Data di pubblicazione Autore(i) File
Collagen VII gene delivery via an Adeno-Sleeping Beauty transposon in COL7A1-deficient keratinocytes from epidermolysis bullosa patients 1-gen-2014 Latella, Maria Carmela; Cocchiarella, Fabienne; Turchiano, Giandomenico; Gonçalves, Manuel; Larcher3, Fernando; Izsvak, Zsuzsanna; Ivics, Zoltan; Recchia, Alessandra
Collagen VII gene delivery via Sleeping Beauty transposon in COL7A1-deficient keratinocytes from epidermolysis bullosa patients 1-gen-2013 Latella, Maria Carmela; Cocchiarella, Fabienne; Turchiano, Giandomenico; Gonçalves, Manuel; Larcher, Fernando; Mavilio, Fulvio; Izsvak, Zsuzsanna; Ivics, Zoltan; Recchia, Alessandra
CRISPR/Cas9-Based Disease Modeling and Functional Correction of Interleukin 7 Receptor Alpha Severe Combined Immunodeficiency in T-Lymphocytes and Hematopoietic Stem Cells 1-gen-2024 Rai, R.; Steinberg, Z.; Romito, M.; Zinghirino, F.; Hu, Y. -T.; White, N.; Naseem, A.; Thrasher, A. J.; Turchiano, G.; Cavazza, A.
Development of a Sleeping Beauty transposon-based integration system for gene transfer in human epithelial cells 1-gen-2011 Turchiano, Giandomenico; Latella, Maria Carmela; Izsvak, Zsuzsanna; Ivics, Zoltan; Mavilio, Fulvio; Recchia, Alessandra
Dominant and recessive mutations in rhodopsin activate different cell death pathways 1-gen-2016 Comitato, Antonella; DI SALVO, MARIA TERESA; Turchiano, Giandomenico; Montanari, Monica; Sakami, Sanae; Palczewski, Krzysztof; Marigo, Valeria
Engineered nucleases-mediated in situ correction of a genetic defect by homologous recombination into the native locus 1-gen-2015 Latella, Maria Carmela; Miselli, Francesca; Turchiano, Giandomenico; Mussolino, Claudio; Cudeiro, Javier; Larcher, Fernando; Recchia, Alessandra
Erratum: Genomic analysis of sleeping beauty transposon integration in human somatic cells (PLoS ONE (2014) 9:11 (e112712) DOI: 10.1371/journal.pone.0112712) 1-gen-2020 Turchiano, G.; Latella, M. C.; Doring, A. G.; Cattoglio, C.; Mavilio, F.; Izsvak, Z.; Ivics, Z.; Recchia, A.
Gene Editing and Genotoxicity: Targeting the Off-Targets 1-gen-2020 Blattner, G.; Cavazza, A.; Thrasher, A. J.; Turchiano, G.
Genomic Analysis of Sleeping Beauty Transposon Integration in Human Somatic Cells 1-gen-2014 Turchiano, Giandomenico; Latella, Maria Carmela; Gogol Doring, Andreas; Cattoglio, Claudia; Mavilio, Fulvio; Izsvak, Zsuzsanna; Ivics, Zoltan; Recchia, Alessandra
Hematopoietic stem cell gene editing rescues B-cell development in X-linked agammaglobulinemia 1-gen-2024 Bahal, Sameer; Zinicola, Marta; E Moula, Shefta; Whittaker, Thomas E.; Schejtman, Andrea; Naseem, Asma; Blanco, Elena; Vetharoy, Winston; Hu, Yi-Ting; Rai, Rajeev; Gomez-Castaneda, Eduardo; Cunha-Santos, Catarina; Burns, Siobhan O.; Morris, Emma C.; Booth, Claire; Turchiano, Giandomenico; Cavazza, Alessia; Thrasher, Adrian J.; Santilli, Giorgia
Non viral gene transfer via Sleeping beauty transposon for Collagen VII delivery in human primary keratinocytes. 1-gen-2012 Latella, Maria Carmela; Turchiano, Giandomenico; Cocchiarella, Fabienne; Izsvak, Zsuzsanna; Ivics, Zoltan; Mavilio, Fulvio; Recchia, Alessandra
Pigment epithelium-derived factor hinders photoreceptor cell death by reducing intracellular calcium in the degenerating retina 1-gen-2018 Comitato, Antonella; Subramanian, Preeti; Turchiano, Giandomenico; Montanari, Monica; Becerra, S. Patricia; Marigo, Valeria
Progress and harmonization of gene editing to treat human diseases: Proceeding of COST Action CA21113 GenE-HumDi 1-gen-2023 Cavazza, A.; Hendel, A.; Bak, R. O.; Rio, P.; Guell, M.; Lainscek, D.; Arechavala-Gomeza, V.; Peng, L.; Hapil, F. Z.; Harvey, J.; Ortega, F. G.; Gonzalez-Martinez, C.; Lederer, C. W.; Mikkelsen, K.; Gasiunas, G.; Kalter, N.; Goncalves, M. A. F. V.; Petersen, J.; Garanto, A.; Montoliu, L.; Maresca, M.; Seemann, S. E.; Gorodkin, J.; Mazini, L.; Sanchez, R.; Rodriguez-Madoz, J. R.; Maldonado-Perez, N.; Laura, T.; Schmueck-Henneresse, M.; Maccalli, C.; Grunewald, J.; Carmona, G.; Kachamakova-Trojanowska, N.; Miccio, A.; Martin, F.; Turchiano, G.; Cathomen, T.; Luo, Y.; Tsai, S. Q.; Benabdellah, K.
Targeted gene correction of human hematopoietic stem cells for the treatment of Wiskott - Aldrich Syndrome 1-gen-2020 Rai, R.; Romito, M.; Rivers, E.; Turchiano, G.; Blattner, G.; Vetharoy, W.; Ladon, D.; Andrieux, G.; Zhang, F.; Zinicola, M.; Leon-Rico, D.; Santilli, G.; Thrasher, A. J.; Cavazza, A.