CAVAZZA, ALESSIA

CAVAZZA, ALESSIA  

Dipartimento di Scienze Mediche e Chirurgiche Materno-Infantili e dell'Adulto  

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Advanced delivery systems for gene editing: A comprehensive review from the GenE-HumDi COST Action Working Group 1-gen-2025 Cavazza, Alessia; Molina-Estévez, Francisco J; Reyes, Álvaro Plaza; Ronco, Victor; Naseem, Asma; Malenšek, Špela; Pečan, Peter; Santini, Annalisa; Heredia, Paula; Aguilar-González, Araceli; Boulaiz, Houria; Ni, Qianqian; Cortijo-Gutierrez, Marina; Pavlovic, Kristina; Herrera, Inmaculada; de la Cerda, Berta; Garcia-Tenorio, Emilio M; Richard, Eva; Granados-Principal, Sergio; López-Márquez, Arístides; Köber, Mariana; Stojanovic, Marijana; Vidaković, Melita; Santos-Garcia, Irene; Blázquez, Lorea; Haughton, Emily; Yan, Dongnan; Sánchez-Martín, Rosario María; Mazini, Loubna; Aseguinolaza, Gloria Gonzalez; Miccio, Annarita; Rio, Paula; Desviat, Lourdes R; Gonçalves, Manuel A F V; Peng, Ling; Jiménez-Mallebrera, Cecilia; Molina, Francisco Martin; Gupta, Dhanu; Lainšček, Duško; Luo, Yonglun; Benabdellah, Karim
An improved medium formulation for efficient ex vivo gene editing, expansion and engraftment of hematopoietic stem and progenitor cells 1-gen-2023 Rai, R.; Naseem, A.; Vetharoy, W.; Steinberg, Z.; Thrasher, A. J.; Santilli, G.; Cavazza, A.
Ascl2-Dependent Cell Dedifferentiation Drives Regeneration of Ablated Intestinal Stem Cells 1-gen-2020 Murata, K.; Jadhav, U.; Madha, S.; van Es, J.; Dean, J.; Cavazza, A.; Wucherpfennig, K.; Michor, F.; Clevers, H.; Shivdasani, R. A.
CRISPR/Cas9-Based Disease Modeling and Functional Correction of Interleukin 7 Receptor Alpha Severe Combined Immunodeficiency in T-Lymphocytes and Hematopoietic Stem Cells 1-gen-2024 Rai, R.; Steinberg, Z.; Romito, M.; Zinghirino, F.; Hu, Y. -T.; White, N.; Naseem, A.; Thrasher, A. J.; Turchiano, G.; Cavazza, A.
Dynamic Transcriptional and Epigenetic Regulation of Human Epidermal Keratinocyte Differentiation 1-gen-2016 Cavazza, Alessia; Miccio, Annarita; Romano, Oriana; Petiti, Luca; Malagoli Tagliazucchi, Guidantonio; Peano, Clelia; Severgnini, Marco; Rizzi, Ermanno; De Bellis, Gianluca; Bicciato, Silvio; Mavilio, Fulvio
Enhancer, transcriptional, and cell fate plasticity precedes intestinal determination during endoderm development 1-gen-2018 Banerjee, K. K.; Saxena, M.; Kumar, N.; Chen, L.; Cavazza, A.; Toke, N. H.; O'Neill, N. K.; Madha, S.; Jadhav, U.; Verzi, M. P.; Shivdasani, R. A.
Enhancing Lentiviral and Alpharetroviral Transduction of Human Hematopoietic Stem Cells for Clinical Application 1-gen-2019 Schott, J. W.; Leon-Rico, D.; Ferreira, C. B.; Buckland, K. F.; Santilli, G.; Armant, M. A.; Schambach, A.; Cavazza, A.; Thrasher, A. J.
Extensive Recovery of Embryonic Enhancer and Gene Memory Stored in Hypomethylated Enhancer DNA 1-gen-2019 Jadhav, U.; Cavazza, A.; Banerjee, K. K.; Xie, H.; O'Neill, N. K.; Saenz-Vash, V.; Herbert, Z.; Madha, S.; Orkin, S. H.; Zhai, H.; Shivdasani, R. A.
Gene Editing and Genotoxicity: Targeting the Off-Targets 1-gen-2020 Blattner, G.; Cavazza, A.; Thrasher, A. J.; Turchiano, G.
Gene Editing for the Treatment of Primary Immunodeficiency Diseases 1-gen-2021 Rai, R.; Thrasher, A. J.; Cavazza, A.
Gene therapy of skin adhesion disorders (mini review) 1-gen-2012 Cavazza, Alessia; Mavilio, Fulvio
Genome editing for blood disorders: State of the art and recent advances 1-gen-2019 Romito, M.; Rai, R.; Thrasher, A. J.; Cavazza, A.
Genome editing for primary immunodeficiencies: A therapeutic perspective on Wiskott-Aldrich syndrome 1-gen-2022 Naseem, A.; Steinberg, Z.; Cavazza, A.
Hematopoietic stem cell gene editing rescues B-cell development in X-linked agammaglobulinemia 1-gen-2024 Bahal, Sameer; Zinicola, Marta; E Moula, Shefta; Whittaker, Thomas E.; Schejtman, Andrea; Naseem, Asma; Blanco, Elena; Vetharoy, Winston; Hu, Yi-Ting; Rai, Rajeev; Gomez-Castaneda, Eduardo; Cunha-Santos, Catarina; Burns, Siobhan O.; Morris, Emma C.; Booth, Claire; Turchiano, Giandomenico; Cavazza, Alessia; Thrasher, Adrian J.; Santilli, Giorgia
It's all about location: Targeting the right spot for Wiskott-Aldrich syndrome 1-gen-2024 Naseem, A.; Cavazza, A.
Mechanisms of retroviral integration and mutagenesis 1-gen-2013 Cavazza, Alessia; Moiani, Arianna; Mavilio, Fulvio
Multidimensional Response Surface Methodology for the Development of a Gene Editing Protocol for p67phox-Deficient Chronic Granulomatous Disease 1-gen-2024 Whittaker, T. E.; Moula, S. E.; Bahal, S.; Bakri, F. G.; Hayajneh, W. A.; Daoud, A. K.; Naseem, A.; Cavazza, A.; Thrasher, A. J.; Santilli, G.
Progress and harmonization of gene editing to treat human diseases: Proceeding of COST Action CA21113 GenE-HumDi 1-gen-2023 Cavazza, A.; Hendel, A.; Bak, R. O.; Rio, P.; Guell, M.; Lainscek, D.; Arechavala-Gomeza, V.; Peng, L.; Hapil, F. Z.; Harvey, J.; Ortega, F. G.; Gonzalez-Martinez, C.; Lederer, C. W.; Mikkelsen, K.; Gasiunas, G.; Kalter, N.; Goncalves, M. A. F. V.; Petersen, J.; Garanto, A.; Montoliu, L.; Maresca, M.; Seemann, S. E.; Gorodkin, J.; Mazini, L.; Sanchez, R.; Rodriguez-Madoz, J. R.; Maldonado-Perez, N.; Laura, T.; Schmueck-Henneresse, M.; Maccalli, C.; Grunewald, J.; Carmona, G.; Kachamakova-Trojanowska, N.; Miccio, A.; Martin, F.; Turchiano, G.; Cathomen, T.; Luo, Y.; Tsai, S. Q.; Benabdellah, K.
Self-inactivating MLV vectors have a reduced genotoxic profile in human epidermal keratinocytes 1-gen-2013 Cavazza, A.; Cocchiarella, F.; Bartholomae, C.; Schmidt, M.; Pincelli, C.; Larcher, F.; Mavilio, F.
Single-Cell Transcript Profiles Reveal Multilineage Priming in Early Progenitors Derived from Lgr5+ Intestinal Stem Cells 1-gen-2016 Kim, T. -H.; Saadatpour, A.; Guo, G.; Saxena, M.; Cavazza, A.; Desai, N.; Jadhav, U.; Jiang, L.; Rivera, M. N.; Orkin, S. H.; Yuan, G. -C.; Shivdasani, R. A.