Sfoglia per Autore
In vitro and in vivo CRISPR/Cas9-mediated genome editing to downregulate dominant mutations in Rhodopsin gene
2016 Benati, Daniela; Latella, Maria Carmela; DI SALVO, MARIA TERESA; Cocchiarella, Fabienne; Marigo, Valeria; Recchia, Alessandra
Transcriptionally regulated and nontoxic delivery of the hyperactive Sleeping Beauty Transposase
2016 Cocchiarella, Fabienne; Latella, Maria Carmela; Basile, Valentina; Miselli, Francesca; Galla, Melanie; Imbriano, Carol; Recchia, Alessandra
In vitro and in vivo genome editing of the RHO gene to downregulate dominant mutations
2016 Marigo, Valeria; Latella, Maria Carmela; DI SALVO, MARIA TERESA; Recchia, Alessandra
In vivo editing of the human mutant Rhodopsin gene by electroporation of plasmid-based CRISPR/Cas9 in the mouse retina
2016 Latella, Maria Carmela; Di Salvo, Maria Teresa; Cocchiarella, Fabienne; Benati, Daniela; Grisendi, Giulia; Comitato, Antonella; Marigo, Valeria; Recchia, Alessandra
CRISPR/Cas9-mediated specific knock-down of dominant mutations in Rhodopsin gene
2017 Benati, Daniela; Manel, Llado; Patrizi, Clarissa; Schiroli, Davide; Marigo, Valeria; Auricchio, Alberto; Recchia, Alessandra
Closure of a Large Chronic Wound through Transplantation of Gene-Corrected Epidermal Stem Cells
2017 Bauer, Johann; Koller, Josef; Murauer, Eva; DE ROSA, Laura; Enzo, Elena; Carulli, Sonia; Bondanza, Sergio; Recchia, Alessandra; Muss, Wolfgang; Diem, Anja; Mayr, Elisabeth; Schlager, Pamina; Gratz, Iris; Pellegrini, Graziella; DE LUCA, Michele
Transcriptional and epigenetic analyses of the DMD locus reveal novel cisâ acting DNA elements that govern muscle dystrophin expression
2017 Gherardi, Samuele; Bovolenta, Matteo; Passarelli, Chiara; Falzarano, Maria Sofia; Pigini, Paolo; Scotton, Chiara; Neri, Marcella; Armaroli, Annarita; Osman, Hana; Selvatici, Rita; Gualandi, Francesca; Recchia, Alessandra; Mora, Marina; Bernasconi, Pia; Maggi, Lorenzo; Morandi, Lucia; Ferlini, Alessandra; Perini, Giovanni
Correction of recessive dystrophic epidermolysis bullosa by transposon-mediated integration of COL7A1 in transplantable patient-derived primary keratinocytes.
2017 Latella, Maria Carmela; Cocchiarella, Fabienne; De Rosa, Laura; Turchiano, Giandomenico; Gonçalves, Manuel; Larcher, Fernando; De Luca, Michele; Recchia, Alessandra
Specific knock-down of C-terminal dominant mutation in Rhodopsin gene by CRISPR/Cas9 system
2018 Benati, Daniela; Patrizi, Clarissa; Marigo, Valeria; Auricchio, Alberto; Recchia, Alessandra
An efficient in vitro transposition method by a transcriptionally regulated sleeping beauty system packaged into an integration defective lentiviral vector
2018 Benati, Daniela; Cocchiarella, Fabienne; Recchia, Alessandra
Bimodal CD40/Fas-Dependent Crosstalk between iNKT Cells and Tumor-Associated Macrophages Impairs Prostate Cancer Progression
2018 Cortesi, Filippo; Delfanti, Gloria; Grilli, Andrea; Calcinotto, Arianna; Gorini, Francesca; Pucci, Ferdinando; Lucianò, Roberta; ` Grioni, Matteo; Recchia, Alessandra; Benigni, Fabio; Briganti, Alberto; Salonia, Andrea; De Palma, Michele; Bicciato, Silvio; Doglioni, Claudio; Bellone, Matteo; Casorati, Giulia; Dellabona, Paolo.
Efficient CRISPR/Cas9-Mediated iIn Situ Correction of LAMB3 Gene in Keratinocytes Derived from Junctional Epidermolysis Bullosa Patient
2018 Benati, Daniela; Miselli, Francesca; Cocchiarella, Fabienne; Patrizi, Clarissa; Latella, Maria Carmela; Baldassarri, Samantha; Pedrazzoli, Eleonora; Ammendola, Virginia; Larcher, Fernando; Recchia, Alessandra
CRISPR/Cas9-Mediated In Situ Correction of LAMB3 Gene in Keratinocytes Derived from a Junctional Epidermolysis Bullosa Patient
2018 Benati, Daniela; Miselli, Francesca; Cocchiarella, Fabienne; Patrizi, Clarissa; Carretero, Marta; Baldassarri, Samantha; Ammendola, Virginia; Has, Cristina; Colloca, Stefano; Del Rio, Marcela; Larcher, Fernando; Recchia, Alessandra
Inducible Caspase9-mediated suicide gene for MSC-based cancer gene therapy
2019 Rossignoli, Filippo; Grisendi, Giulia; Spano, Carlotta; Golinelli, Giulia; Recchia, Alessandra; Rovesti, Giulia; Orsi, Giulia; Veronesi, Elena; Horwitz, Edwin M.; Dominici, Massimo
MSC-delivered soluble TRAIl and paclitaxel as novel combinatory treatment for pancreatic adenocarcinoma
2019 Rossignoli, Filippo; Spano, Carlotta; Grisendi, Giulia; Foppiani, Elisabetta Manuela; Golinelli, Giulia; Mastrolia, Ilenia; Bestagno, Marco; Candini, Olivia; Petrachi, Tiziana; Recchia, Alessandra; Miselli, Francesca; Rovesti, Giulia; Orsi, Giulia; Veronesi, Elena; Medici, Gregorio; Petocchi, Benedetta; Pinelli, Massimo; Horwitz, Edwin M.; Conte, Pierfranco; Dominici, Massimo
CRISPR/Cas9 gene editing in vitro and in retinal cells in vivo
2019 Benati, D.; Marigo, V.; Recchia, A.
Soluble TRAIL Armed Human MSC As Gene Therapy For Pancreatic Cancer
2019 Spano, Carlotta; Grisendi, Giulia; Golinelli, Giulia; Rossignoli, Filippo; Prapa, Malvina; Bestagno, Marco; Candini, Olivia; Petrachi, Tiziana; Recchia, Alessandra; Miselli, Francesca; Rovesti, Giulia; Orsi, Giulia; Maiorana, Antonino; Manni, Paola; Veronesi, Elena; Piccinno, Maria Serena; Murgia, Alba; Pinelli, Massimo; Horwitz, Edwin M.; Cascinu, Stefano; Conte, Pierfranco; Dominici, Massimo
AAV-CRISPR Persistence in the Eye of the Beholder
2019 Recchia, A.
Gene editing prospects for treating inherited retinal diseases
2020 Benati, D.; Patrizi, C.; Recchia, A.
Specific Knock-down of P347S Dominant Mutation in Rhodopsin Gene by CRISPR/Cas9 System
2020 Patrizi, Clarissa; Llado, Manel; Benati, Daniela; Guarascio, Rosellina; Cheetham, Mike; Auricchio, Alberto; Recchia, Alessandra
Titolo | Data di pubblicazione | Autore(i) | File |
---|---|---|---|
In vitro and in vivo CRISPR/Cas9-mediated genome editing to downregulate dominant mutations in Rhodopsin gene | 1-gen-2016 | Benati, Daniela; Latella, Maria Carmela; DI SALVO, MARIA TERESA; Cocchiarella, Fabienne; Marigo, Valeria; Recchia, Alessandra | |
Transcriptionally regulated and nontoxic delivery of the hyperactive Sleeping Beauty Transposase | 1-gen-2016 | Cocchiarella, Fabienne; Latella, Maria Carmela; Basile, Valentina; Miselli, Francesca; Galla, Melanie; Imbriano, Carol; Recchia, Alessandra | |
In vitro and in vivo genome editing of the RHO gene to downregulate dominant mutations | 1-gen-2016 | Marigo, Valeria; Latella, Maria Carmela; DI SALVO, MARIA TERESA; Recchia, Alessandra | |
In vivo editing of the human mutant Rhodopsin gene by electroporation of plasmid-based CRISPR/Cas9 in the mouse retina | 1-gen-2016 | Latella, Maria Carmela; Di Salvo, Maria Teresa; Cocchiarella, Fabienne; Benati, Daniela; Grisendi, Giulia; Comitato, Antonella; Marigo, Valeria; Recchia, Alessandra | |
CRISPR/Cas9-mediated specific knock-down of dominant mutations in Rhodopsin gene | 1-gen-2017 | Benati, Daniela; Manel, Llado; Patrizi, Clarissa; Schiroli, Davide; Marigo, Valeria; Auricchio, Alberto; Recchia, Alessandra | |
Closure of a Large Chronic Wound through Transplantation of Gene-Corrected Epidermal Stem Cells | 1-gen-2017 | Bauer, Johann; Koller, Josef; Murauer, Eva; DE ROSA, Laura; Enzo, Elena; Carulli, Sonia; Bondanza, Sergio; Recchia, Alessandra; Muss, Wolfgang; Diem, Anja; Mayr, Elisabeth; Schlager, Pamina; Gratz, Iris; Pellegrini, Graziella; DE LUCA, Michele | |
Transcriptional and epigenetic analyses of the DMD locus reveal novel cisâ acting DNA elements that govern muscle dystrophin expression | 1-gen-2017 | Gherardi, Samuele; Bovolenta, Matteo; Passarelli, Chiara; Falzarano, Maria Sofia; Pigini, Paolo; Scotton, Chiara; Neri, Marcella; Armaroli, Annarita; Osman, Hana; Selvatici, Rita; Gualandi, Francesca; Recchia, Alessandra; Mora, Marina; Bernasconi, Pia; Maggi, Lorenzo; Morandi, Lucia; Ferlini, Alessandra; Perini, Giovanni | |
Correction of recessive dystrophic epidermolysis bullosa by transposon-mediated integration of COL7A1 in transplantable patient-derived primary keratinocytes. | 1-gen-2017 | Latella, Maria Carmela; Cocchiarella, Fabienne; De Rosa, Laura; Turchiano, Giandomenico; Gonçalves, Manuel; Larcher, Fernando; De Luca, Michele; Recchia, Alessandra | |
Specific knock-down of C-terminal dominant mutation in Rhodopsin gene by CRISPR/Cas9 system | 1-gen-2018 | Benati, Daniela; Patrizi, Clarissa; Marigo, Valeria; Auricchio, Alberto; Recchia, Alessandra | |
An efficient in vitro transposition method by a transcriptionally regulated sleeping beauty system packaged into an integration defective lentiviral vector | 1-gen-2018 | Benati, Daniela; Cocchiarella, Fabienne; Recchia, Alessandra | |
Bimodal CD40/Fas-Dependent Crosstalk between iNKT Cells and Tumor-Associated Macrophages Impairs Prostate Cancer Progression | 1-gen-2018 | Cortesi, Filippo; Delfanti, Gloria; Grilli, Andrea; Calcinotto, Arianna; Gorini, Francesca; Pucci, Ferdinando; Lucianò, Roberta; ` Grioni, Matteo; Recchia, Alessandra; Benigni, Fabio; Briganti, Alberto; Salonia, Andrea; De Palma, Michele; Bicciato, Silvio; Doglioni, Claudio; Bellone, Matteo; Casorati, Giulia; Dellabona, Paolo. | |
Efficient CRISPR/Cas9-Mediated iIn Situ Correction of LAMB3 Gene in Keratinocytes Derived from Junctional Epidermolysis Bullosa Patient | 1-gen-2018 | Benati, Daniela; Miselli, Francesca; Cocchiarella, Fabienne; Patrizi, Clarissa; Latella, Maria Carmela; Baldassarri, Samantha; Pedrazzoli, Eleonora; Ammendola, Virginia; Larcher, Fernando; Recchia, Alessandra | |
CRISPR/Cas9-Mediated In Situ Correction of LAMB3 Gene in Keratinocytes Derived from a Junctional Epidermolysis Bullosa Patient | 1-gen-2018 | Benati, Daniela; Miselli, Francesca; Cocchiarella, Fabienne; Patrizi, Clarissa; Carretero, Marta; Baldassarri, Samantha; Ammendola, Virginia; Has, Cristina; Colloca, Stefano; Del Rio, Marcela; Larcher, Fernando; Recchia, Alessandra | |
Inducible Caspase9-mediated suicide gene for MSC-based cancer gene therapy | 1-gen-2019 | Rossignoli, Filippo; Grisendi, Giulia; Spano, Carlotta; Golinelli, Giulia; Recchia, Alessandra; Rovesti, Giulia; Orsi, Giulia; Veronesi, Elena; Horwitz, Edwin M.; Dominici, Massimo | |
MSC-delivered soluble TRAIl and paclitaxel as novel combinatory treatment for pancreatic adenocarcinoma | 1-gen-2019 | Rossignoli, Filippo; Spano, Carlotta; Grisendi, Giulia; Foppiani, Elisabetta Manuela; Golinelli, Giulia; Mastrolia, Ilenia; Bestagno, Marco; Candini, Olivia; Petrachi, Tiziana; Recchia, Alessandra; Miselli, Francesca; Rovesti, Giulia; Orsi, Giulia; Veronesi, Elena; Medici, Gregorio; Petocchi, Benedetta; Pinelli, Massimo; Horwitz, Edwin M.; Conte, Pierfranco; Dominici, Massimo | |
CRISPR/Cas9 gene editing in vitro and in retinal cells in vivo | 1-gen-2019 | Benati, D.; Marigo, V.; Recchia, A. | |
Soluble TRAIL Armed Human MSC As Gene Therapy For Pancreatic Cancer | 1-gen-2019 | Spano, Carlotta; Grisendi, Giulia; Golinelli, Giulia; Rossignoli, Filippo; Prapa, Malvina; Bestagno, Marco; Candini, Olivia; Petrachi, Tiziana; Recchia, Alessandra; Miselli, Francesca; Rovesti, Giulia; Orsi, Giulia; Maiorana, Antonino; Manni, Paola; Veronesi, Elena; Piccinno, Maria Serena; Murgia, Alba; Pinelli, Massimo; Horwitz, Edwin M.; Cascinu, Stefano; Conte, Pierfranco; Dominici, Massimo | |
AAV-CRISPR Persistence in the Eye of the Beholder | 1-gen-2019 | Recchia, A. | |
Gene editing prospects for treating inherited retinal diseases | 1-gen-2020 | Benati, D.; Patrizi, C.; Recchia, A. | |
Specific Knock-down of P347S Dominant Mutation in Rhodopsin Gene by CRISPR/Cas9 System | 1-gen-2020 | Patrizi, Clarissa; Llado, Manel; Benati, Daniela; Guarascio, Rosellina; Cheetham, Mike; Auricchio, Alberto; Recchia, Alessandra |
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