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Titolo Data di pubblicazione Autore(i) File
Site-specific integration by the adeno-associated virus rep protein 1-gen-2011 Recchia, Alessandra; Mavilio, Fulvio
Targeted gene integration in human epidermal stem cells by Zinc-finger nuclease-mediated homologous recombination. 1-gen-2012 Coluccio, Andrea; Lombardo, Angelo; Miselli, Francesca; Holmes, Michael; Gregory, Philip D.; Naldini, Luigi; Recchia, Alessandra; Mavilio, Fulvio
Non viral gene transfer via Sleeping beauty transposon for Collagen VII delivery in human primary keratinocytes. 1-gen-2012 Latella, Maria Carmela; Turchiano, Giandomenico; Cocchiarella, Fabienne; Izsvak, Zsuzsanna; Ivics, Zoltan; Mavilio, Fulvio; Recchia, Alessandra
Collagen VII gene delivery via Sleeping Beauty transposon in COL7A1-deficient keratinocytes from epidermolysis bullosa patients 1-gen-2013 Latella, Maria Carmela; Cocchiarella, Fabienne; Turchiano, Giandomenico; Gonçalves, Manuel; Larcher, Fernando; Mavilio, Fulvio; Izsvak, Zsuzsanna; Ivics, Zoltan; Recchia, Alessandra
Transcriptionally regulated and non-toxic delivery of the hyperactive Sleeping Beauty Transposase 1-gen-2013 Cocchiarella, Fabienne; Latella, Maria Carmela; Basile, Valentina; Galla, Melanie; Imbriano, Carol; Ivics, Zoltan; Izsvak, Zsuzsanna; Recchia, Alessandra
IL-7 and IL-15 instruct the generation of human memory stem T cells from naïve precursors 1-gen-2013 N., Cieri; B., Camisa; Cocchiarella, Fabienne; Forcato, Mattia; G., Oliveira; E., Provasi; A., Bondanza; C., Bordignon; J., Peccatori; F., Ciceri; M. T., Lupo Stanghellini; Mavilio, Fulvio; A., Mondino; Bicciato, Silvio; Recchia, Alessandra; C., Bonini
Genotoxic signature in cord blood cells of newborns exposed in utero to a zidovudine-based antiretroviral combination 1-gen-2013 Isabelle Andre, Schmutz; Liliane Dal, Cortivo; Emmanuelle, Six; Sophie, Kaltenbach; Fabienne, Cocchiarella; Jerome Le, Chenadec; Nicolas, Cagnard; Anne Gael, Cordier; Alexandra, Benachi; Laurent, Mandelbrot; Elie, Azria; Naima, Bouallag; Sonia, Luce; Brigitte, Ternaux; Christian, Reimann; Patrick, Revy; Isabelle Radford, Weiss; Cristina, Leschi; Recchia, Alessandra; Mavilio, Fulvio; Marina Cavazzana, Calvo*; Stéphane, Blanche
Differential integrity of TALE nuclease genes following adenoviral and lentiviral vector gene transfer into human cells 1-gen-2013 Holkers, M; Maggio, I; Liu, J; Janssen, Jm; Miselli, F; Mussolino, C; Recchia, Alessandra; Cathomen, T; Gonçalves, Ma
Targeted integration of a large transgene cassette by TALEN and ZFN-mediated homologous recombination. 1-gen-2013 Marchetti, Marco; Miselli, Francesca; Holkers, Maarten; Mussolino, Claudio; Gonçalves, Manuel; Cathomen, Toni; Recchia, Alessandra
Targeted Gene Addition in Human Epithelial Stem Cells by Zinc-finger Nuclease-mediated Homologous Recombination 1-gen-2013 Coluccio, Andrea; Miselli, Francesca; Angelo, Lombardo; Marconi, Alessandra; Guidantonio Malagoli, Tagliazucchi; Manuel A., Gonçalves; Pincelli, Carlo; Giulietta, Maruggi; Marcela Del, Rio; Luigi, Naldini; Fernando, Larcher; Mavilio, Fulvio; Recchia, Alessandra
Collagen VII gene delivery via an Adeno-Sleeping Beauty transposon in COL7A1-deficient keratinocytes from epidermolysis bullosa patients 1-gen-2014 Latella, Maria Carmela; Cocchiarella, Fabienne; Turchiano, Giandomenico; Gonçalves, Manuel; Larcher3, Fernando; Izsvak, Zsuzsanna; Ivics, Zoltan; Recchia, Alessandra
TALEN-mediated in situ correction of a genetic defect by homologous recombination into the native locus 1-gen-2014 Miselli, Francesca; Marchetti, Marco; Mussolino, Claudio; Cudeiro, Javier; Larcher, Fernando; Recchia, Alessandra
Genomic Analysis of Sleeping Beauty Transposon Integration in Human Somatic Cells 1-gen-2014 Turchiano, Giandomenico; Latella, Maria Carmela; Gogol Doring, Andreas; Cattoglio, Claudia; Mavilio, Fulvio; Izsvak, Zsuzsanna; Ivics, Zoltan; Recchia, Alessandra
Long-Term Skin Regeneration From a Gene-Targeted Human Epidermal Stem Cell Clone 1-gen-2014 Duarte, Blanca; Miselli, Francesca; Murillas, Rodolfo; Espinosa Hevia, Luis; Cruz Cigudosa, Juan; Recchia, Alessandra; Del Río, Marcela; Larcher, Fernando
Long-term stability and safety of transgenic cultured epidermal stem cells in gene therapy of junctional epidermolysis bullosa. 1-gen-2014 DE ROSA, Laura; Carulli, S; Cocchiarella, Fabienne; Quaglino, Daniela; Enzo, Elena; Franchini, Eleonora; Giannetti, A; DE SANTIS, Giorgio; Recchia, Alessandra; Pellegrini, Graziella; DE LUCA, Michele
Nuclear architecture dictates HIV-1 integration site selection 1-gen-2015 Marini, Bruna; Kertesz Farkas, Attila; Ali, Hashim; Lucic, Bojana; Lisek, Kamil; Manganaro, Lara; Pongor, Sandor; Luzzati, Roberto; Recchia, Alessandra; Mavilio, Fulvio; Giacca, Mauro; Lusic, Marina
A single epidermal stem cell strategy for safe ex vivo gene therapy 1-gen-2015 Droz‐Georget Lathion, Stéphanie; Rochat, Ariane; Knott, Graham; Recchia, Alessandra; Martinet, Danielle; Benmohammed, Sara; Grasset, Nicolas; Zaffalon, Andrea; Besuchet Schmutz, Nathalie; Savioz‐dayer, Emmanuelle; Beckmann, Jacques Samuel; Rougemont, Jacques; Mavilio, Fulvio; Barrandon, Yann
Engineered nucleases-mediated in situ correction of a genetic defect by homologous recombination into the native locus 1-gen-2015 Latella, Maria Carmela; Miselli, Francesca; Turchiano, Giandomenico; Mussolino, Claudio; Cudeiro, Javier; Larcher, Fernando; Recchia, Alessandra
Design of a regulated lentiviral vector for hematopoietic stem cell gene therapy of globoid cell leukodystrophy 1-gen-2015 Ungari, S.; Montepeloso, A.; Morena, F.; Cocchiarella, Fabienne; Recchia, Alessandra; Martino, S.; Gentner, B.; Naldini, L.; Biffi, A.
In vitro and in vivo genome editing of the RHO gene to downregulate dominant mutations 1-gen-2016 Latella, Maria C.; Di Salvo, Maria T.; Cocchiarella, Fabienne; Benati, Daniela; Marigo, Valeria; Recchia, Alessandra
Mostrati risultati da 21 a 40 di 73
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