LATELLA, Maria Carmela

LATELLA, Maria Carmela  

Dipartimento di Scienze della Vita  

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Titolo Data di pubblicazione Autore(i) File
Allele specific CRISPR/Cas9 editing of dominant Epidermolysis Bullosa Simplex in human epidermal stem cells 1-gen-2023 Cattaneo, C; Enzo, E; De Rosa, L; Sercia, L; Consiglio, F; Forcato, M; Bicciato, S; Paiardini, A; Basso, G; Tagliafico, E; Paganelli, A; Fiorentini, C; Magnoni, C; Latella, M C; De Luca, M
Collagen VII gene delivery via an Adeno-Sleeping Beauty transposon in COL7A1-deficient keratinocytes from epidermolysis bullosa patients 1-gen-2014 Latella, Maria Carmela; Cocchiarella, Fabienne; Turchiano, Giandomenico; Gonçalves, Manuel; Larcher3, Fernando; Izsvak, Zsuzsanna; Ivics, Zoltan; Recchia, Alessandra
Collagen VII gene delivery via Sleeping Beauty transposon in COL7A1-deficient keratinocytes from epidermolysis bullosa patients 1-gen-2013 Latella, Maria Carmela; Cocchiarella, Fabienne; Turchiano, Giandomenico; Gonçalves, Manuel; Larcher, Fernando; Mavilio, Fulvio; Izsvak, Zsuzsanna; Ivics, Zoltan; Recchia, Alessandra
Correction of recessive dystrophic epidermolysis bullosa by transposon-mediated integration of COL7A1 in transplantable patient-derived primary keratinocytes. 1-gen-2017 Latella, Maria Carmela; Cocchiarella, Fabienne; De Rosa, Laura; Turchiano, Giandomenico; Gonçalves, Manuel; Larcher, Fernando; De Luca, Michele; Recchia, Alessandra
Development of a Sleeping Beauty transposon-based integration system for gene transfer in human epithelial cells 1-gen-2011 Turchiano, Giandomenico; Latella, Maria Carmela; Izsvak, Zsuzsanna; Ivics, Zoltan; Mavilio, Fulvio; Recchia, Alessandra
Efficient CRISPR/Cas9-Mediated iIn Situ Correction of LAMB3 Gene in Keratinocytes Derived from Junctional Epidermolysis Bullosa Patient 1-gen-2018 Benati, Daniela; Miselli, Francesca; Cocchiarella, Fabienne; Patrizi, Clarissa; Latella, Maria Carmela; Baldassarri, Samantha; Pedrazzoli, Eleonora; Ammendola, Virginia; Larcher, Fernando; Recchia, Alessandra
Engineered nucleases-mediated in situ correction of a genetic defect by homologous recombination into the native locus 1-gen-2015 Latella, Maria Carmela; Miselli, Francesca; Turchiano, Giandomenico; Mussolino, Claudio; Cudeiro, Javier; Larcher, Fernando; Recchia, Alessandra
Erratum: Genomic analysis of sleeping beauty transposon integration in human somatic cells (PLoS ONE (2014) 9:11 (e112712) DOI: 10.1371/journal.pone.0112712) 1-gen-2020 Turchiano, G.; Latella, M. C.; Doring, A. G.; Cattoglio, C.; Mavilio, F.; Izsvak, Z.; Ivics, Z.; Recchia, A.
Genomic Analysis of Sleeping Beauty Transposon Integration in Human Somatic Cells 1-gen-2014 Turchiano, Giandomenico; Latella, Maria Carmela; Gogol Doring, Andreas; Cattoglio, Claudia; Mavilio, Fulvio; Izsvak, Zsuzsanna; Ivics, Zoltan; Recchia, Alessandra
In vitro and in vivo CRISPR/Cas9-mediated genome editing to downregulate dominant mutations in Rhodopsin gene 1-gen-2016 Benati, Daniela; Latella, Maria Carmela; DI SALVO, MARIA TERESA; Cocchiarella, Fabienne; Marigo, Valeria; Recchia, Alessandra
In vitro and in vivo genome editing of the RHO gene to downregulate dominant mutations 1-gen-2016 Latella, Maria C.; Di Salvo, Maria T.; Cocchiarella, Fabienne; Benati, Daniela; Marigo, Valeria; Recchia, Alessandra
In vitro and in vivo genome editing of the RHO gene to downregulate dominant mutations 1-gen-2016 Marigo, Valeria; Latella, Maria Carmela; DI SALVO, MARIA TERESA; Recchia, Alessandra
In vivo editing of the human mutant Rhodopsin gene by electroporation of plasmid-based CRISPR/Cas9 in the mouse retina 1-gen-2016 Latella, Maria Carmela; Di Salvo, Maria Teresa; Cocchiarella, Fabienne; Benati, Daniela; Grisendi, Giulia; Comitato, Antonella; Marigo, Valeria; Recchia, Alessandra
Non viral gene transfer via Sleeping beauty transposon for Collagen VII delivery in human primary keratinocytes. 1-gen-2012 Latella, Maria Carmela; Turchiano, Giandomenico; Cocchiarella, Fabienne; Izsvak, Zsuzsanna; Ivics, Zoltan; Mavilio, Fulvio; Recchia, Alessandra
Transcriptionally regulated and non-toxic delivery of the hyperactive Sleeping Beauty Transposase 1-gen-2013 Cocchiarella, Fabienne; Latella, Maria Carmela; Basile, Valentina; Galla, Melanie; Imbriano, Carol; Ivics, Zoltan; Izsvak, Zsuzsanna; Recchia, Alessandra
Transcriptionally regulated and nontoxic delivery of the hyperactive Sleeping Beauty Transposase 1-gen-2016 Cocchiarella, Fabienne; Latella, Maria Carmela; Basile, Valentina; Miselli, Francesca; Galla, Melanie; Imbriano, Carol; Recchia, Alessandra