Sfoglia per Rivista GENE THERAPY
Metabolically stabilized long-circulating PEGylated polyacridine peptide polyplexes mediate hydrodynamically stimulated gene expression in liver
2011 Fernandez, C. A.; Baumhover, N. J.; Duskey, J. T.; Khargharia, S.; Kizzire, K.; Ericson, M. D.; Rice, K. G.
Risk assessment in skin gene therapy: Viral-cellular fusion transcripts generated by proviral transcriptional read-through in keratinocytes transduced with self-inactivating lentiviral vectors
2011 Almarza, D.; Bussadori, G.; Navarro, M.; Mavilio, F.; Larcher, F.; Murillas, R.
Self-inactivating MLV vectors have a reduced genotoxic profile in human epidermal keratinocytes
2013 Cavazza, A.; Cocchiarella, F.; Bartholomae, C.; Schmidt, M.; Pincelli, C.; Larcher, F.; Mavilio, F.
The importance of epidermal stem cells in keratinocyte-mediated gene therapy
1997 De Luca, Michele; Pellegrini, Graziella
The uptake mechanism of PEGylated DNA polyplexes by the liver influences gene expression
2014 Khargharia, S.; Baumhover, N. J.; Crowley, S. T.; Duskey, J.; Rice, K. G.
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