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Towards the correction of genetic defect in corneal keratinocytes from patient with macular corneal Dystrophy type II 1-gen-2004 Ferrari, S; Ferrari, G; Rossi, C; Miccio, Annarita; Volpi, Nicola; Mavilio, Fulvio; Pellegrini, Graziella; De, Luca
Hot spots of retroviral integrations in human CD34+ hematopoietic cells 1-gen-2007 Cattoglio, C; Facchini, Giulia; Sartori, D; Antonelli, A; Miccio, Annarita; Cassani, B; Schmidt, M; VON KALLE, C; Howe, S; Thrasher, A. J.; Aiuti, A; Ferrari, G; Recchia, Alessandra; Mavilio, Fulvio
Transcription factor binding sites are genetic determinants of retroviral integration in the human genome. 1-gen-2009 Felice, B; Cattoglio, C; Cittaro, D; Testa, Anna; Miccio, Annarita; Ferrari, G; Luzi, L; Recchia, Alessandra; Mavilio, Fulvio
Lentiviral vector integration in the human genome induces alternative splicing and generates aberrant transcripts 1-gen-2012 Moiani, Arianna; Paleari, Ylenia; Sartori, Daniela; Mezzadra, Riccardo; Miccio, Annarita; Cattoglio, Claudia; Cocchiarella, Fabienne; Lidonnici, Maria Rosa; Ferrari, Giuliana; Mavilio, Fulvio
Deletion of the LTR Enhancer/Promoter Has No Impact on the Integration Profile of MLV Vectors in Human Hematopoietic Progenitors 1-gen-2013 Moiani, A.; Miccio, A.; Rizzi, E.; Severgnini, M.; Pellin, D.; Suerth, J. D.; Baum, C.; de Bellis, G.; Mavilio, F.
Genome-wide definition of promoter and enhancer usage during neural induction of human embryonic stem cells 1-gen-2015 Poletti, Valentina; Delli Carri, Alessia; Malagoli Tagliazucchi, Guidantonio; Faedo, Andrea; Petiti, Luca; Mazza, Emilia Maria Cristina; Peano, Clelia; De Bellis, Gianluca; Bicciato, Silvio; Miccio, Annarita; Cattaneo, Elena; Mavilio, Fulvio
Concise Review: Epigenetic Regulation of Hematopoiesis: Biological Insights and Therapeutic Applications 1-gen-2017 Antoniani, Chiara; Romano, Oriana; Miccio, Annarita
Induction of fetal hemoglobin synthesis by CRISPR/Cas9-mediated editing of the human b-globin locus 1-gen-2018 Antoniani, C.; Meneghini, V.; Lattanzi, A.; Felix, T.; Romano, O.; Magrin, E.; Weber, L.; Pavani, G.; Hoss, S. E.; Kurita, R.; Nakamura, Y.; Cradick, T. J.; Lundberg, A. S.; Porteus, M.; Amendola, M.; Nemer, W. E.; Cavazzana, M.; Mavilio, F.; Miccio, A.
An Optimized Lentiviral Vector Efficiently Corrects the Human Sickle Cell Disease Phenotype 1-gen-2018 Weber, L.; Poletti, V.; Magrin, E.; Antoniani, C.; Martin, S.; Bayard, C.; Sadek, H.; Felix, T.; Meneghini, V.; Antoniou, M. N.; El-Nemer, W.; Mavilio, F.; Cavazzana, M.; Andre-Schmutz, I.; Miccio, A.
Plerixafor enables the safe, rapid, efficient mobilization of haematopoietic stem cells in sickle cell disease patients after exchange transfusion 1-gen-2018 Lagresle-Peyrou, Chantal; Lefrère, François; Magrin, Elisa; Ribeil, Jean-Antoine; Romano, Oriana; Weber, Leslie; Magnani, Alessandra; Sadek, Hanem; Plantier, Clémence; Gabrion, Aurélie; Ternaux, Brigitte; Félix, Tristan; Couzin, Chloé; Stanislas, Aurélie; Tréluyer, Jean-Marc; Lamhaut, Lionel; Joseph, Laure; Delville, Marianne; Miccio, Annarita; André-Schmutz, Isabelle; Cavazzana, Marina
Optimization of CRISPR/Cas9 Delivery to Human Hematopoietic Stem and Progenitor Cells for Therapeutic Genomic Rearrangements 1-gen-2019 Lattanzi, Annalisa; Meneghini, Vasco; Pavani, Giulia; Amor, Fatima; Ramadier, Sophie; Felix, Tristan; Antoniani, Chiara; Masson, Cecile; Alibeu, Olivier; Lee, Ciaran; Porteus, Matthew H.; Bao, Gang; Amendola, Mario; Mavilio, Fulvio; Miccio, Annarita
GATA factor transcriptional activity: Insights from genome-wide binding profiles 1-gen-2020 Romano, O.; Miccio, A.
Base-editing-mediated dissection of a γ-globin cis-regulatory element for the therapeutic reactivation of fetal hemoglobin expression 1-gen-2022 Antoniou, P.; Hardouin, G.; Martinucci, P.; Frati, G.; Felix, T.; Chalumeau, A.; Fontana, L.; Martin, J.; Masson, C.; Brusson, M.; Maule, G.; Rosello, M.; Giovannangeli, C.; Abramowski, V.; de Villartay, J. -P.; Concordet, J. -P.; Del Bene, F.; El Nemer, W.; Amendola, M.; Cavazzana, M.; Cereseto, A.; Romano, O.; Miccio, A.
Progress and harmonization of gene editing to treat human diseases: Proceeding of COST Action CA21113 GenE-HumDi 1-gen-2023 Cavazza, A.; Hendel, A.; Bak, R. O.; Rio, P.; Guell, M.; Lainscek, D.; Arechavala-Gomeza, V.; Peng, L.; Hapil, F. Z.; Harvey, J.; Ortega, F. G.; Gonzalez-Martinez, C.; Lederer, C. W.; Mikkelsen, K.; Gasiunas, G.; Kalter, N.; Goncalves, M. A. F. V.; Petersen, J.; Garanto, A.; Montoliu, L.; Maresca, M.; Seemann, S. E.; Gorodkin, J.; Mazini, L.; Sanchez, R.; Rodriguez-Madoz, J. R.; Maldonado-Perez, N.; Laura, T.; Schmueck-Henneresse, M.; Maccalli, C.; Grunewald, J.; Carmona, G.; Kachamakova-Trojanowska, N.; Miccio, A.; Martin, F.; Turchiano, G.; Cathomen, T.; Luo, Y.; Tsai, S. Q.; Benabdellah, K.
Mostrati risultati da 1 a 14 di 14
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